
Epilepsy
Epilepsy is one of the most common and disabling chronic neurological disorders and currently affects more than 50 million people worldwide. There is a significant medical need as approximately 30 percent of patients are insensitive to treatment by conventional epilepsy medicines.
Hypothalamic obesity
“Life with HO feels a bit like you’re alone under a cloudy sky feeling very little hope but… you always keep your lifeline out as far as you can reaching for any possibilities.”
Erin, mother of Jesse a hypothalamic obesity survivor

Prader-Willi syndrome
“PWS means I’m special and I have to eat healthy. I don’t like being special.”
John, living with PWS


Rare diseases
Did you know there are more than 7,000 known rare diseases, but less than 10% have treatments? Learn more about the unmet need in rare disease…