Improve the lives of rare disease patients around the world through scientific innovation.
We leverage our ion channel targeting expertise to discover, develop and deliver innovative rare disease treatments.
Our Core Values
Put People First
Treat all people with kindness, respect and equity. Enable everyone to feel a sense of belonging and live their best life.
Innovation with Impact
Push boundaries with courage. Never give up. And, in the end, deliver excellence.
Maintain the highest ethical standards in all that we do as we deliver with urgency for patients in need.