(tesofensine + metoprolol)
*Voluntarily paused, subject to additional funding
- Prader-Willi syndrome*
- Hypothalamic Obesity*
(GABA α3 PAM)
- Rare neuropathic disorders
(KCa3.1 channel blocker)
- Rare inflammatory and fibrotic disorders
What does it take to develop a drug?
What is a clinical trial? What are the phases of clinical development? And how is this process sometimes different for rare diseases?